Innovative biotechnology in the clinical phase through the development of a gene therapy platform, which targets genetic and rare diseases of the retina for which no solution currently exists.
A 1st product HORA-RPE65 was administered in humans with promising results for treating Leber’s amaurosis with a 3 years follow-up after treatment. A second product targeting retinitis pigmentosa will enter clinical trials in early 2017.
Horama’s team, originating from two research laboratories in Nantes and Montpellier, was the first in France to lead an eye gene therapy trial and produce a clinical batch of GMP adeno‑associated viral vectors.
Gene therapy dedicated to ophthalmology to restore visual function.
At the creation of Horama, Atlanpole brought us real support and assistance as well as many introductions to various partners. Since then, the Atlanpole Biotherapies cluster has helped us to participate in major international conferences in the best conditions and has provided real visibility to our new releases.
To provide therapeutic solutions to prevent blindness.